Lysosomal Disease Program Harvard Medical School
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  Welcome to the Lysosomal Storage Disease website
 

The following website is an educational resource for people dealing with lysosomal storage disorders (LSDs). There are more than 40 diseases classified as LSDs, each caused by a problem with a particular enzyme in the body. While individually each of these diseases are relatively rare,  grouped together they affect 1 in about every 7,700 babies born.

Symptoms vary widely across the different LSDs--some of which may cause relatively minor problems, while others can be very serious. Medical management options for the LSDs often cross several medical specialties. Some LSDs have disease-specific treatment options to consider. Be sure to speak with your doctor about the best medical care options for you or your loved ones.